1 / 4

CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008

CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008. Organized by: RettSearch Sponsored by: International Rett Syndrome Foundation. CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008. CONTEXT.

luana
Download Presentation

CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008

An Image/Link below is provided (as is) to download presentation Download Policy: Content on the Website is provided to you AS IS for your information and personal use and may not be sold / licensed / shared on other websites without getting consent from its author. Content is provided to you AS IS for your information and personal use only. Download presentation by click this link. While downloading, if for some reason you are not able to download a presentation, the publisher may have deleted the file from their server. During download, if you can't get a presentation, the file might be deleted by the publisher.

E N D

Presentation Transcript

  1. CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008 Organized by: RettSearch Sponsored by: International Rett Syndrome Foundation

  2. CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008 CONTEXT Follow up of 2006 San Francisco meeting was needed for discussing multi-center initiatives and the future of RettSearch. The Rett community is growing: new clinics and more scientists (opportunities for translational research). Merge of IRSA and RSRF into IRSF provided opportunity. IRSF is committed to patient-based research. Mini-symposium format allows the identification of key issues. Next meeting will be expanded. Potential industry partners and new clinic centers are present.

  3. CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008 GOALS 1. To determine where we are in terms of: • Carrying out multi-center RTT clinical trials. • Introducing new therapies for RTT. 2. To develop a document stating the meeting’s: • Conclusions (diagnosis). • Recommendations (treatment). 3. To publish Conclusions & Recommendations of meeting and full-length? papers (J Child Neurol).

  4. CLINICAL TRIALS IN RETT SYNDROME A Mini-Symposium Chicago, June 22-23, 2008 AGENDA 1. Target population: who should be treated?a) Genotype-phenotype correlations b) Natural history studies 2. Outcome targets: what to measure?a) Rating scales b) Other measures 3. Treatment targets: what to use? • Prior experiences. • New and promising therapeutic agents.

More Related