Hemophilia Gene Therapy Market Size Projected to be Resilient by 2026

1. Hemophilia Gene Therapy Hemophilia Gene Therapy Market Size, Share, Trend, Outlook, Future Growth Share, Trend, Outlook, Future Growth Analysis And Synthesis 2018 - 2026 Analysis And Synthesis 2018 - 2026 Market Size, Hemophilia is a genetic bleeding disorder in which an individual lacks or has low levels of proteins called clotting factors. There are around 13 types of clotting factors that work with blood platelets, which are necessary for clotting process to initiate. There are three forms of hemophilia - A, B, and C. Hemophilia A is the most common form and is caused due to deficiency in clotting factor VIII. Hemophilia B occurs due to deficiency of clotting factor IX and Hemophilia C is caused due to clotting factor XI deficiency. Hemophilia is incurable with current therapeutic options, which only reduces symptoms such as spontaneous bleeding in muscles and joints as well as increased risk for intracranial hemorrhage. These treatment options lasts only for a day and is costly. As against conventional clotting factor replacement therapy, gene therapy is expected to offer sustainable cure for hemophilia by correcting defective gene sequence (F8 or F9 gene) that codes for clotting factor VIII or IX in the patient’s body. Request Free Sample Copy @ Request Free Sample Copy @ https://www.coherentmarketinsights.com/insight/request-sample/2480 https://www.coherentmarketinsights.com/insight/request-sample/2480 The global hemophilia gene therapy market was valued at US$ 0.00 million in 2017 and is expected to The global hemophilia gene therapy market was valued at US$ 0.00 million in 2017 and is expected to witness a CAGR of 56.0% over the forecast period (2018 – 2026). witness a CAGR of 56.0% over the forecast period (2018 – 2026). Increasing hemophilia patient base worldwide especially in developed countries is expected to drive Increasing hemophilia patient base worldwide especially in developed countries is expected to drive growth of the hemophilia gene therapy market growth of the hemophilia gene therapy market High prevalence of hemophilia is increasing demand for sustainable treatment of the disease, which is projected to drive the market growth over the forecast period. According to the National Hemophilia Foundation factsheet 2018, hemophilia affected over 400,000 individuals worldwide. Moreover, according to same source, an estimated 75% of patients suffering from hemophilia have no access to treatment or receive inadequate treatment. According to the Centers for Disease Control and Prevention (CDC) report, Hemophilia A occurs in 1 out of 5,000 live male births. It is around four times more common than

2. Hemophilia B. Few effective treatments available for hemophilia require lifetime infusion of expensive drugs manufactured through recombinant biotechnology or from human plasma. Strong gene-based product pipeline for hemophilia treatment is expected to drive the hemophilia gene Strong gene-based product pipeline for hemophilia treatment is expected to drive the hemophilia gene therapy market growth therapy market growth Gene therapy for hemophilia has strong product pipeline, which is expected to enter the market in the near future. This is expected to drive the market growth, as it would result in availability of new treatment options for management of hemophilia. By Januarys 2019, over 15 investigational gene therapy are under the clinical development stage. In December 2018, Spark Therapeutics announced updated preliminary data for the ongoing phase 1/2 clinical trial of investigational SPK-8011 in hemophilia A. Current therapies for treating hemophilia are only symptomatic management of the disease by administering clotting factors XIII or IX. Furthermore, there are serious adverse effects associated with plasma derived products, and limited access to treatment. Gene therapy may address these issues to certain level. BioMarin Pharmaceutical’s gene therapy product Valoctocogene roxaparvovec for hemophilia A is in phase III of clinical development in 2019. Regulatory bodies such as the U.S. Food and Drug Administration (FDA) are supporting the product development for gene therapy by allotting breakthrough designation status to investigational gene therapy. For instance, in 2017, the U.S. FDA granted breakthrough therapy designation to valoctocogene roxaparvovec, which is an Adeno -associated virus 5 factor VIII vector designed to restore factor VIII plasma concentrations in patients with hemophilia A. Report includes chapters which deeply display the following deliverable about industry : Report includes chapters which deeply display the following deliverable about industry : • Hemophilia Gene Therapy Market Research Objective and Assumption • Hemophilia Gene Therapy Market Purview - Report Description, Executive Summary, and Coherent Opportunity Map (COM) • Hemophilia Gene Therapy Market Dynamics, Regulations, and Trends Analysis - Market Dynamics, Regulatory Scenario, Industry Trend, Merger and Acquisitions, New system Launch/Approvals, Value Chain Analysis, Porter’s Analysis, and PEST Analysis • Global Hemophilia Gene Therapy Market, By Regions • Hemophilia Gene Therapy Market Competition by Manufacturers including Production, Share, Revenue, Average Price, Manufacturing Base Distribution, Sales Area and Product Type. • Hemophilia Gene Therapy Market Manufacturers Profiles/Analysis including Company Basic Information, Manufacturing Base and Its Competitors.

3. • Hemophilia Gene Therapy Market Manufacturing Cost Analysis including Key Raw Materials and Key Suppliers of Raw Materials. • Industrial Chain, Sourcing Strategy and Downstream Buyers including Upstream Raw Materials Sourcing and Downstream Buyers • Marketing Strategy Analysis, Distributors/Traders including Marketing Channel, Market Positioning and Distributors/Traders List. • Market Effect Factors Analysis including Technology Progress/Risk, Consumer Needs/Customer Preference Change and Economic/Political Environmental Change. • Hemophilia Gene Therapy Market Forecast including Production, Consumption, Import and Export Forecast by Type, Applications and Region. • Research Findings and Conclusion Key players operating in the global hemophilia gene therapy market include BioMarin Pharmaceuticals, Inc., Spark Therapeutics, Pfizer, Inc., UniQure NV, Ultragenyx Pharmaceutical, Shire PLC Sangamo Therapeutics, Inc., and Freeline Therapeutics. Detailed Segmentation: Detailed Segmentation: Global Hemophilia Gene Therapy Market, By Type: Global Hemophilia Gene Therapy Market, By Type: Hemophilia A • Hemophilia B • Global Hemophilia Gene Therapy Market, By Region: Global Hemophilia Gene Therapy Market, By Region: North America • Latin America • Europe • Asia Pacific • Middle East • Africa • Look Insights Of Global Hemophilia Gene Therapy Market Research Report At Look Insights Of Global Hemophilia Gene Therapy Market Research Report At https://www.coherentmarketinsights.com/market-insight/hemophilia-gene-therapy-market-2480 https://www.coherentmarketinsights.com/market-insight/hemophilia-gene-therapy-market-2480

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