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COST Action BM1207

Networking towards clinical application of antisense-mediated exon skipping Involving all key stakeholders (clinicians, scientists, industry, patients & regulators) Facilitate the clinical development of antisense-mediated exon skipping for rare diseases

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COST Action BM1207

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  1. Networking towards clinical application of antisense-mediated exon skipping Involving all key stakeholders (clinicians, scientists, industry, patients & regulators) • Facilitate the clinical development of antisense-mediated exon skipping for rare diseases • Exploit exon skipping for as many patients as possible Objectives • Achieve consensus biochemical outcome measures • New regulatory models to allow testing of personalized medicine approaches • Foster synergistic work (workshops and key stakeholder meetings and exchange visits) • Address therapeutic misconception by training early stage researchers Current parties involved: Belgium, Denmark, Estonia, France, Germany, Israel, Italy, Malta, Netherlands, Norway, Portugal, Serbia, Spain, Sweden and United Kingdom If you are interested to join, please contact the Chair of this Action Annemieke Aartsma-Rus, a.m.rus@lumc.nl COST Action BM1207

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